Search for Clinical Trial Results
Amyloid Neuropathies, Familial - 22 Studies Found
Status | Study |
Completed |
Study Name: The Effect of Diflunisal on Familial Transthyretin Amyloidosis Condition: Amyloidosis Date: 2011-09-09 Interventions: Drug: Diflunisal Film-coated tablet, 250 mg twice daily, orally for approximately 2 years |
Completed |
Study Name: Safety, Efficacy and Pharmacokinetics of Doxycycline Plus Tauroursodeoxycholic Acid in Transthyretin Amyloidosis Condition: Transthyretin Amyloidosis Date: 2010-07-27 Interventions: Drug: Doxycycline + Tauroursodeoxycholic acid doxycycline 100 mg twice a day for 12 months; tauroursodeo |
Recruiting |
Study Name: Transthyretin-Associated Amyloidoses Outcome Survey (THAOS) Condition:
Date: 2008-02-25 Interventions: Other: None. Observational Study. |
Completed |
Study Name: ENDEAVOUR: Phase 3 Multicenter Study of Revusiran (ALN-TTRSC) in Patients With Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC) Condition:
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Completed |
Study Name: The Effects of Fx-1006A on Transthyretin Stabilization and Clinical Outcome Measures in Patients With Non-V30M Transthyretin Amyloidosis Condition: Transthyretin-associated Amyloidosis With Polyneuropathy Date: 2008-02-27 Interventions: Drug: Fx-1006A During Part 1, patients will receive Fx-1006A 20mg soft gelatin capsules once daily (at t |
Completed |
Study Name: Safety and Efficacy Study of Doxycycline/UrsoDeoxyCholicAcid on Disease Progression in ATTR Amyloidosis Condition:
Date: 2012-04-19 Interventions:
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Recruiting |
Study Name: Carpal Tunnel Syndrome and Amyloid Cardiomyopathy Condition:
Date: 2016-04-20 |
Recruiting |
Study Name: Prevalence and Post-surgical Outcomes of CARdiac Wild-type TransthyrEtin amyloidoSIs in Elderly Patients With Aortic steNosis Referred for Valvular Replacement. Condition:
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Recruiting |
Study Name: A Safety and Tolerability Study of an Investigational Drug, ALN-TTRSC02, in Healthy Subjects Condition: Transthyretin-mediated Amyloidosis (ATTR Amyloidosis) Date: 2016-05-18 Interventions:
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